I thought the hardest part of this journey would be to find a cure and a treatment for my son,” Andrew Jedlicka told The Post ...
St. Louis Families Unite for Rare Disease Day 2026 as Take Part Foundation Advances Critical Genetic Testing and ...
Exclusive: One in four wait at least three years for diagnosis and many face treatment ‘access lottery’, according to report ...
FDA moves to help those with rare diseases, think twice before at-home genetic testing and a little-known eating disorder ...
During the Boston Globe’s Rare Disease Summit, Dr. Wendy Chung, a physician-scientist and geneticist who leads the Department ...
Scientists have found that a special component in some people's blood provides them with natural protection against malaria. A recent study has demonstrated that a genetic variant named rs112233623-T ...
The FDA guidelines aim to create a new pathway for bespoke therapies due to the challenges of conducting large studies.
The definition of a “rare” disease is based on how often they occur in the population not by whether or not there is a ...
A mother from Belleville hopes to raise awareness about Lafora body disease, an ultra-rare disease her son is battling that ...
The Food and Drug Administration is making it possible for pharmaceutical companies to produce bespoke medicines for individual patients, an effort to revolutionize the standard of care for rare ...