"Gene editing takes centre stage in FDA’s new rare disease approval pathway" was originally created and published by ...
After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...
Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders ...
Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...
Crispr’s ability to cut genetic code like scissors has just started to turn into medicines. Now, gene editing pioneer ...
After dumping its sole remaining gene therapy asset last year, Pfizer has decided to exercise its option for global rights to Beam Therapeutics’ liver-targeted gene editing candidate.
TSRA-196 is designed to precisely correct the genetic mutation underlying AATD, with the goal of restoring production of functional alpha-1 antitrypsin (AAT) protein through a one-time, durable ...
The framework, first introduced by FDA Commissioner Marty Makary and Center for Biologics Evaluation and Research head Vinay ...
Gene editing has enormous potential to help feed the world’s growing population, but it’s currently difficult, time-consuming ...
In this webinar, researchers discuss using and improving next-generation gene editing approaches for targeted, accurate, and ...
A version of this Priestley Medal address will be presented at the American Chemical Society Spring 2026 meeting ...
Scientists achieved the smell by editing genes in tomatoes responsible for their aroma to make them smell similar to popcorn.