Gene editing takes centre stage in FDA’s new rare disease approval pathway

"Gene editing takes centre stage in FDA’s new rare disease approval pathway" was originally created and published by ...

Engineers sharpen gene-editing tools to target cystic fibrosis

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

Gene Editing Has Struggled To Go Commercial. This Nobel Laureate Has A $1 Billion Plan To Fix That.

Crispr’s ability to cut genetic code like scissors has just started to turn into medicines. Now, gene editing pioneer ...

Gene editing treatments could get easier FDA approval under new plan

FDA Commissioner Marty Makary says the agency wants to remove barriers for patients suffering from rare genetic conditions.

New targeted base-editing tool corrects genetic brain disorder in mice

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

Studies test whether gene-editing can fix high cholesterol. For now, take your medicine

Today there are injected medicines that block proteins produced by the PCSK9 and ANGPTL3 genes in the liver, thus helping the ...
BioSpace

FDA’s Bespoke Pathway To Focus on Gene Editing and RNA-Based Treatments for Rare Diseases

The framework, first introduced by FDA Commissioner Marty Makary and Center for Biologics Evaluation and Research head Vinay ...
University of California, Davis

A Gene Editor That's a Better Fit for Plants

Gene editing has enormous potential to help feed the world’s growing population, but it’s currently difficult, time-consuming ...

Stronger scents and healthier crops: Unlocking plants' hidden potential through precision gene editing

Scientists have long sought to understand why some plants are fragrant powerhouses while others remain subtle. Now, a ...
MedPage Today on MSN

Studies Test Whether Gene-Editing Can Fix High Cholesterol

Two companies show hints that switching off certain genes could dramatically lower cholest ...
Frontiers

Gene editing in vaccine development against vectors and vector-borne diseases (VBDs)

Vector-borne diseases (VBDs) represent a critical challenge in infectious disease control due to their complex transmission dynamics, diverse vector ...
News-Medical.Net on MSN

Engineers develop highly precise gene editor for safer cystic fibrosis treatments

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic "base pairs" to a new level of precision, opening the door to safer, more ...