Rare Disease Advisor, a trusted source of medical news and feature content for healthcare providers, offers clinicians insight into the latest research to inform clinical practice and improve patient ...

The project addresses a long-standing gap in the field: the lack of a clear human reference standard for muscle regeneration. A new research collaboration between muscular dystrophy organizations aims ...

The updated AABB/ICTMG guideline hopes to decrease excessive platelet transfusions. The adoption of an updated, more restrictive 2025 Association for the Advancement ...

HDFN can cause adverse outcomes both prenatally and postnatally. Hemolytic disease of the fetus and newborn (HDFN) can be associated with both severe pre- and postnatal outcomes, according to a study ...

New research suggests that caffeine could help treat fatigue, among the most troubling symptoms of multiple sclerosis (MS). According to the results of a small study published in the February 2026 ...

Multivariate analysis revealed several factors that affected overall survival, including a diagnosis of NF1, evidence of metastasis at diagnosis, the maximum diameter of the primary tumor at diagnosis ...

Nintedanib significantly reduced the decline in the forced vital capacity of patients with progressive pulmonary fibrosis (PPF). Treatment with nintedanib significantly slows the progression of ...

Chimeric antigen receptor (CAR) T cells based on the proximal region of mesothelin completely eradicated CCA tumors in 3 different mouse models. Mesothelin, a tumor differentiation antigen that is ...

Unexplained anemia and hyperbilirubinemia in a patient with syncope prompted further evaluation, leading to the diagnosis of warm AIHA associated with RSV infection. A young woman presenting to the ...

Obstructive sleep apnea prevalence increased in children with achondroplasia beginning at school age (6-12 years) and remained elevated into adolescence. Recurrent otitis media may accompany ...

Life expectancy in DMD has improved over time. Previous estimates pointed to a life expectancy of 25 years, with more recent data reporting a life expectancy of 31.7 years (95% CI, 27.4-36.0). 3,4 A ...

At present, no validated tools or scoring systems have been developed to predict prognosis or clinical course of warm autoimmune hemolytic anemia (AIHA). Several potential prognostic risk factors that ...