"Gene editing takes centre stage in FDA’s new rare disease approval pathway" was originally created and published by ...

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

The framework, first introduced by FDA Commissioner Marty Makary and Center for Biologics Evaluation and Research head Vinay ...

FDA Commissioner Marty Makary says the agency wants to remove barriers for patients suffering from rare genetic conditions.

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

Gene editing has enormous potential to help feed the world’s growing population, but it’s currently difficult, time-consuming ...

Scientists have long sought to understand why some plants are fragrant powerhouses while others remain subtle. Now, a ...

The Food and Drug Administration aims to evaluate treatments for rare diseases based on plausible evidence that they would ...

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic "base pairs" to a new level of precision, opening the door to safer, more ...

UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene ...