History gathering should solicit the patient’s abilities or limitations with these activities of daily living (ADLs). The patient may have mild arthralgias. Lungs are the most common extra muscular ...
WVE-N531 showed significant improvements in functional measures and muscle health in DMD patients during the phase 2 FORWARD-53 trial. Sustained exon skipping, dystrophin restoration, and improved ...
Many patients are given a different diagnosis initially, including lupus erythematous and undifferentiated connective tissue disease. It is of paramount importance to determine the organ (i.e. skin, ...