Genetic disorders occur due to alterations in the primary genetic material, deoxyribonucleic acid (DNA), of an organism.
Picture CRISPR-Cas9, a gene editing technology, as a GPS-guided scalpel: gRNA directs the Cas9 enzyme, a protein that cuts ...
Scientists say they have used the gene-editing tool CRISPR inside someone's body for the first time, a new frontier for efforts to operate on DNA, the chemical code of life, to treat diseases. A ...
Innovative research into the gene-editing tool targets influenza’s ability to replicate—stopping it in its tracks.
CRISPR, short for Clustered Regularly Interspaced Short Palindromic Repeats, is a revolutionary gene-editing tool originally discovered as a bacterial defence mechanism. Scientists have repurposed it ...
A bacterial defense system called SPARDA employs kamikaze-like tactics to protect cells and could be useful in future ...
Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...
A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based gene editing to treat a child with a rare genetic disorder. Unlike earlier ...
CRISPR gene editing revolutionized the cell and gene therapy (CGT) industry this past decade, but the industry still faces significant bottlenecks and gaps between development and manufacturing that ...
Scientists are testing CRISPR gene editing as a potential HIV cure after successfully removing the virus from infected cells ...
As CRISPR moves from lab success to real-world medicine, 2026 will test whether these revolutionary gene-editing therapies ...
Gene editing figures to be part of the future of medicine, but a popular system for it has some room for improvement, researchers say. That’s why a team from UC San Diego in La Jolla set out with Yale ...